Case Studies
Clinical Trial Design for Fibrodysplasia Ossificans Progressiva (FOP)
This project focuses on designing clinical trials for Fibrodysplasia Ossificans Progressiva, a rare and debilitating condition that causes soft tissues to turn into bone.
Health Technology Assessment for Mucopolysaccharidosis (MPS)
This project involves conducting a Health Technology Assessment (HTA) for new treatments targeting Mucopolysaccharidosis, a group of rare metabolic disorders.